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Peptide-conjugate antisense based splice-correction for Duchenne muscular dystrophy and other neuromuscular diseases.
EBioMedicine, 45, 630-645
Citation
Tsoumpra, Maria K; Fukumoto, Seiji; Matsumoto, Toshio; Takeda, Shin'ichi; Wood, Matthew J A; Aoki, Yoshitsugu. (2019). Peptide-conjugate antisense based splice-correction for Duchenne muscular dystrophy and other neuromuscular diseases.. EBioMedicine, 45, 630-645. https://doi.org/10.1016/j.ebiom.2019.06.036